Inborn errors of metabolism
Drug Name
- ALDURAZYME
- AMMONUL
- BUPHENYL POWDER
- BUPHENYL TABLETS
- CARBAGLU
- CARNITOR
- CARNITOR INJECTION
- CARNITOR ORAL SOLUTION
- CARNITOR SF
- CERDELGA
- CEREZYME
- CRYSVITA
- CYCLINEX-1
- CYCLINEX-2
- CYSTADANE
- DOJOLVI
- ELAPRASE
- ELELYSO
- FABRAZYME
- GALAFOLD
- GIVLAARI
- GLASSIA
- KALYDECO
- KALYDECO ORAL GRANULES
- KANUMA
- KUVAN
- KUVAN POWDER
- LUMIZYME
- MEPSEVII
- MSUD ANALOG
- MYALEPT
- MYOZYME
- NAGLAZYME
- NEXVIAZYME
- NITYR
- NULIBRY
- ONPATTRO
- ORFADIN
- ORFADIN ORAL SUSPENSION
- ORKAMBI
- ORKAMBI ORAL GRANULES
- OXLUMO
- PALYNZIQ
- PANHEMATIN
- PROLASTIN-C
- RAVICTI
- REVONTO
- RYANODEX
- SCENESSE
- STRENSIQ
- SYMDEKO
- SYPRINE
- TEGSEDI
- TRIKAFTA
- VIJOICE
- VIMIZIM
- VPRIV
- XURIDEN
- ZAVESCA
- ZEMAIRA
- ZOKINVY
