Oral Ketamine Gets Orphan Drug Status for Rett Syndrome
The Company has completed a phase 2 trial which evaluated the efficacy and safety of oral ketamine in patients with Rett syndrome.
Diagnosis & Disease Information
Polypill Not Linked to Reduced Cognitive Decline in Seniors
But polypill with or without aspirin is associated with reduced functional decline for those aged 65 years or older with cardiovascular risk factors
IVF Not Tied to Worse Developmental, Educational Outcomes
Findings for assessments conducted both at 4 to 6 years and 7 to 9 years versus spontaneously conceived children
Briumvi Now Available for Multiple Sclerosis Treatment
The CD20-directed cytolytic antibody therapy was approved based on data from two phase 3 trials.
Limited Drug Exposure Data Halt Accelerated Approval Attempt for Donanemab
Donanemab is an antibody therapy that targets a modified form of deposited amyloid-β peptide called N3pG.
Web-Based System Works Well for Diagnosis, Treatment of Recurrent Vertigo
Recurrent benign paroxysmal positional vertigo resolved for 72.4 percent of patients using web-based system
Antibody Oligonucleotide Conjugate Fast Tracked for Facioscapulohumeral Muscular Dystrophy
AOC 1020 is designed to reduce the expression of DUX4 mRNA and DUX4 protein in muscles.
MPR Weekly Dose Podcast Episode #144
FDA grant accelerated approval to Alzheimer disease treatment; New fixed-dose asthma treatment; NERD therapy looks promising; Leukemia drug to be withdrawn in 2023; Pertussis prevention treatment approved for use during pregnancy.
Vamorolone Under Review for Duchenne Muscular Dystrophy
Vamorolone is a first-in-class dissociative steroidal drug that retains the anti-inflammatory activity of corticosteroids but with a novel mechanism of action.
