FDA Designates DTX101 Orphan Drug for Hemophilia B

Dimension Therapeutics announced that the Food and Drug Administration (FDA) granted Orphan Drug designation to DTX101 for the treatment of moderate-severe to severe hemophilia B.

Dimension expects to initiate a multi-center phase 1/2 study to evaluate DTX101 in adult patients with moderate-severe to severe hemophilia B by the end of 2015.

RELATED: FDA Designates ACE910 Breakthrough Therapy for Hemophilia A

DTX101 is designed to deliver blood clotting Factor IX (FIX) gene expression in patients with hemophilia B, a rare genetic bleeding disorder resulting from a deficiency in FIX.

For more information call (617) 401–0011 or visit DimensionTx.com.

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